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Endometriosis Drug Pipeline — PatSnap Eureka

Endometriosis Drug Pipeline — PatSnap Eureka
Drug Pipeline Intelligence

Endometriosis Drug Pipeline: GnRH Antagonists, Progesterone Modulators & Anti-Inflammatory Targets

Endometriosis affects an estimated 10–20% of women of reproductive age. The therapeutic landscape is shifting from GnRH agonist paradigms toward oral non-peptide antagonists, next-generation progesterone modulators, and novel anti-inflammatory mechanisms including CGRP/RAMP1 blockade and IL-11 pathway inhibition.

Key Molecular Targets in the Pipeline

Ten distinct targets identified across patent filings in this dataset

Endometriosis Molecular Targets: GnRH Receptor (Advanced/Commercial), PR (Preclinical/Early Clinical), PGE2 EP2/EP4 (Preclinical), MMP-7 (Preclinical), CGRP/RAMP1 (Preclinical), IL-11/IL-11RA (Preclinical), PRLR (Preclinical), SNCG (Preclinical), VEGF/Dopamine (Preclinical), NGF (Preclinical) Overview of ten molecular targets identified in the endometriosis patent landscape, ranging from commercially advanced GnRH receptor antagonists to early-stage anti-inflammatory and anti-angiogenic mechanisms. Source: PatSnap Eureka patent analysis. GnRH Receptor Progesterone R (PR) PGE2 EP2/EP4 MMP-7 CGRP/RAMP1 IL-11/IL-11RA NGF / PRLR / VEGF Advanced Early Clinical Preclinical Preclinical Preclinical Preclinical Preclinical
10–20%
of women of reproductive age affected by endometriosis
10+
distinct molecular targets identified across patent filings
6+
jurisdictions covered by ObsEva linzagolix portfolio alone
2001–2024
patent filing span across the Bayer entity landscape
Disease & Target Overview

An Estrogen-Responsive, Progesterone-Resistant Inflammatory Disease

Endometriosis is consistently framed across retrieved patent filings as an estrogen-responsive and progesterone-unresponsive condition — a characterisation explicitly stated in a Texas A&M University System filing, which establishes progesterone resistance as a defining molecular feature. This mechanistic framing drives the diversity of therapeutic approaches now entering the pipeline.

The disease is characterised by functional endometrial tissue growing outside the uterine cavity, causing dysmenorrhea, menorrhagia, pelvic pain, and reduced fertility. Multiple Jenapharm GmbH & Co. KG and Bayer Schering Pharma filings describe it as a proliferative, hormone-dependent gynecological disorder. According to WHO, endometriosis affects roughly 10% of women of reproductive age globally — though patent-based estimates in this dataset cite 10–20%.

The PatSnap life sciences intelligence platform enables researchers and IP teams to map the full molecular target landscape for conditions like endometriosis, identifying white spaces and freedom-to-operate risks across modalities. Understanding the disease's dual hormonal and inflammatory biology is essential for interpreting the divergent IP strategies documented here.

A 2022 clinical guideline paper from the University of Tokyo Department of Obstetrics and Gynecology documents the real-world transition from GnRH agonist-dominated therapy to dienogest and GnRH antagonist regimens in Japan — providing direct clinical evidence context for the patent signals described in this report.

0.5–100mg
Daily dose range for mesoprogestin J-series compounds
169+ days
Minimum continuous dienogest/cyproterone administration for pain reduction
p<0.0001
Statistical significance of IL-11 antibody uterine weight reduction in mouse models
2024
Year of most recent patent filing in this dataset (CGRP/RAMP1, Children's Medical Center)
  • GnRH receptor — most commercially active target in dataset
  • Progesterone receptor — mechanistically diverse, IP-distinct modalities
  • PGE2 EP2/EP4 — non-hormonal, fertility-preserving claimed advantage
  • MMP-7 — selective in vivo lesion reduction validated
  • CGRP/RAMP1 — migraine agent repurposing signal (2024)
  • IL-11/IL-11RA — immunological non-hormonal target
Therapeutic Modalities

Six Drug Classes Reshaping the Endometriosis Pipeline

From commercially advanced GnRH antagonists to preclinical anti-inflammatory biologics, the pipeline spans hormonal suppression, receptor modulation, and novel immune targets.

Most Active · Advanced/Commercial

Oral Non-Peptide GnRH Antagonists

ObsEva S.A. holds the most concentrated single-assignee portfolio in this dataset, claiming linzagolix (thieno[3,4-d]pyrimidine derivative) across WO, US, AU, SG, JP, and CA. AbbVie Inc. (with Neurocrine Biosciences) claims elagolix sodium formulation IP in IL and SG. Key differentiators include oral bioavailability, AMH/E2 biomarker-guided dosing, and fertility recovery windows via treatment interruption — addressing bone mineral density liabilities of predecessor GnRH agonists.

Linzagolix · Elagolix · Multi-jurisdictional
Historically Dense · Preclinical/Early Clinical

Progesterone Receptor Modulators (Mesoprogestins & SPRMs)

Jenapharm GmbH & Co. KG, Schering Aktiengesellschaft, and Bayer Schering Pharma filings span 2001–2010 across at least 9 jurisdictions. Mesoprogestins (J867, J912, J900, J914, J1042) stabilise PR at an intermediate agonist/antagonist state not reachable by pure progestins or antiprogestins. Bayer Pharma separately claims vilaprisan (SPRM) for endometriosis, fibroids, and meningioma. The J-series IP estate is largely inactive — a potential freedom-to-operate opportunity for next-generation programs.

Mesoprogestins · Vilaprisan · CDB-4124
Clinical Evidence · Paradigm Shift

Gestagen-Class Progestogens (Dienogest)

Bayer Schering Parma claims dienogest at doses up to twice the ovulation-inhibiting dose without bone density loss. Zimmermann, Holger holds a US patent for continuous dienogest or cyproterone acetate for at least 169 days or 25 weeks with demonstrated pain reduction. The 2022 University of Tokyo clinical guideline documents the introduction of dienogest as marking a paradigm shift from GnRH agonist-dominated therapy in Japan — the only direct clinical signal in this dataset. Miscon Trading S.A. additionally claims intralesional progestogen delivery via transvaginal, endoscopic, or laparoscopic routes.

Dienogest · Cyproterone Acetate · Intralesional delivery
Preclinical · Non-Hormonal

Prostaglandin EP2/EP4 Receptor Antagonists

Texas A&M University System and inventor Arosh, Joe A. claim selective inhibition of PGE2 receptors EP2 and EP4 via novel cell signaling mechanisms — purportedly without compromising reproductive function, a key claimed advantage over hormonal approaches. Pfizer Limited filed pyrrolidine and azetidine-based EP2 antagonists (SG, JP, 2011) for endometriosis and uterine fibroids, extending this target into small-molecule drug design. All filings in this class are preclinical with no clinical signals in the retrieved dataset.

EP2 · EP4 · Fertility-preserving claim
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Access the full breakdown of MMP-7, CGRP/RAMP1, IL-11, NGF, and PRLR approaches — including assignee details, preclinical data signals, and white-space analysis.
MMP-7 specificity data CGRP repurposing signals IL-11 p<0.0001 evidence + Anti-NGF & PRLR
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Patent Intelligence

Map freedom-to-operate across every endometriosis modality

Identify inactive IP estates, layered composition-of-matter barriers, and emerging assignee activity across GnRH, PR, and anti-inflammatory drug classes.

Analyse Patent Landscape in Eureka
Pipeline Data Visualisation

Patent Activity & Development Stage Across Therapeutic Classes

Derived from patent and literature signals in this dataset. Development stage is inferred from filing breadth, vintage, and clinical context — not from regulatory submissions.

Key Assignee Jurisdictional Breadth

ObsEva leads with 6 jurisdictions for linzagolix; Bayer entities span the broadest organisational footprint (2001–2022).

Endometriosis Patent Assignee Jurisdictional Breadth: ObsEva S.A. 6 jurisdictions, Bayer entities 10+ jurisdictions (2001–2022), AbbVie/Neurocrine 2 jurisdictions, Miscon Trading 6 jurisdictions, Pfizer Limited 3 jurisdictions, Ferring B.V. 4 jurisdictions Comparison of patent filing jurisdictional breadth for key endometriosis drug pipeline assignees, based on patent records retrieved via PatSnap Eureka. ObsEva S.A. leads in GnRH antagonist multi-jurisdictional prosecution; Bayer entities show the longest historical span. ObsEva S.A. Bayer (all entities) Miscon Trading Ferring B.V. AbbVie/Neurocrine Pfizer Limited 6 jurisdictions 10+ 6 jurisdictions 4 jurisdictions 2 jurisdictions 3 jurisdictions

Pipeline Development Stage Distribution

GnRH antagonists are the only advanced/commercial-stage class; the majority of novel targets remain preclinical.

Endometriosis Pipeline Development Stage: Advanced/Commercial 1 class (GnRH Antagonists), Clinical 1 class (Progestogens/Dienogest), Early Clinical 1 class (Progesterone Receptor Modulators), Preclinical 3+ classes (EP2/EP4, MMP-7, CGRP/RAMP1, IL-11, NGF, PRLR) Distribution of endometriosis drug pipeline therapeutic classes by inferred development stage, based on patent filing breadth, vintage, and clinical context signals retrieved via PatSnap Eureka. Preclinical classes represent the majority of novel mechanism activity. 6 drug classes Advanced/Commercial Clinical Early Clinical Preclinical (majority) EP2/EP4, MMP-7, CGRP, IL-11, NGF, PRLR, SNCG

Patent Filing Timeline by Modality

Mesoprogestin filings begin 2001; CGRP/RAMP1 is the most recently dated filing (2024), signalling an emerging frontier.

Endometriosis Patent Filing Timeline: Mesoprogestins 2001–2010, Progestogens 2008–2022, GnRH Antagonists 2020–2022, EP2/EP4 Antagonists 2010–2011, IL-11/IL-11RA 2022, CGRP/RAMP1 2024 Gantt-style timeline showing the filing span of each endometriosis therapeutic modality from earliest to most recent patent in this dataset, sourced from PatSnap Eureka patent records. The timeline reveals the historical depth of progesterone modulation IP and the emerging 2024 CGRP/RAMP1 frontier. 2000 2010 2020 2025 Mesoprogestins Progestogens GnRH Antagonists EP2/EP4 IL-11/IL-11RA CGRP/RAMP1 2001–2010 2008–2022 2020–2022 2010–2011 2022 2024

Mechanism Category: Hormonal vs. Non-Hormonal Targets

Non-hormonal, mechanism-specific approaches represent the highest-risk/highest-reward frontier — avoiding reproductive axis suppression.

Endometriosis Target Mechanism Categories: Hormonal (GnRH Receptor, PR Modulators, Progestogens, PRLR/Dopamine) vs Non-Hormonal (EP2/EP4, MMP-7, CGRP/RAMP1, IL-11/IL-11RA, NGF, SNCG/VEGF). Hormonal: 4 classes. Non-Hormonal: 6 classes. Categorisation of endometriosis molecular targets into hormonal (reproductive axis-suppressing) and non-hormonal (inflammation/angiogenesis-targeting) mechanisms, based on patent claims retrieved via PatSnap Eureka. Non-hormonal targets now outnumber hormonal targets in this dataset. Hormonal Targets (4) GnRH Receptor Progesterone Receptor (PR) Progestogens (Gestagen class) PRLR / Dopamine (VEGF) Non-Hormonal Targets (6) PGE2 EP2/EP4 Antagonists MMP-7 Monoclonal Antibody CGRP/RAMP1 Blockade IL-11/IL-11RA · NGF · SNCG

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Assignee & IP Landscape

Key Patent-Driving Organisations in the Endometriosis Pipeline

Patent activity is heavily dominant in this dataset. Academic literature is represented by one clinical guideline and one diagnostic biomarker study.

Assignee Primary Target / Modality Key Compounds / Agents Jurisdictions Filing Span Stage (Inferred)
ObsEva S.A. GnRH Receptor Antagonist Linzagolix (thieno[3,4-d]pyrimidine) WO, US, AU, SG, JP, CA 2020–2022 Advanced/Commercial
Bayer (all entities) PR Modulators, SPRMs, Anti-PRLR, IL-11 J-series, Vilaprisan, 005-C04/006-H08 antibodies AU, EP, NO, NZ, SK, BG, TR, RS, WO 2001–2022 Clinical / Preclinical
AbbVie Inc. (+ Neurocrine Biosciences) GnRH Receptor Antagonist Elagolix sodium IL, SG 2020 Advanced/Commercial
Miscon Trading S.A. Progestogens (Intralesional delivery) Progesterone, Gestodene, Norgestimate EP, AU, CA, PL, ES, PH Multiple (inactive) Inactive/Legacy
Texas A&M / Arosh, Joe A. PGE2 EP2/EP4 Receptor Antagonists 6-isopropoxy-9-oxoxanthene-2-carboxylic acid (EP2); morpholine cyclopentyl heptenoic acid (EP4) US, WO 2010 Preclinical
Pfizer Limited EP2 Antagonists, NGF Antagonists Pyrrolidines, Azetidines SG, JP, WO, CA 2010–2011 Preclinical/Legacy
Ferring B.V. Anti-Angiogenic (Dopamine D2 agonist) Quinagolide WO, US, PL, EP Multiple Preclinical
Children's Medical Center Corporation CGRP/RAMP1 Signaling Rimegepant, Fremanezumab, Galcanezumab WO 2024 Preclinical (IND-enabling)
Yeda Research & Development Co. Ltd MMP-7 Selective Antibody Anti-MMP-7 monoclonal antibody IL (pending) 2023 Preclinical

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Strategic Intelligence

Key Strategic Implications for Drug Developers & IP Teams

Derived from patent filing patterns, assignee activity, and translational signals identified in this dataset.

⚖️

GnRH Antagonist IP Is Layered and Contested

ObsEva S.A. holds multi-jurisdictional linzagolix filings through 2022, while AbbVie/Neurocrine claims elagolix formulation IP. Companies entering this space face layered composition-of-matter and formulation patent barriers. Freedom-to-operate due diligence is required, particularly for oral non-peptide thieno[3,4-d]pyrimidine chemotypes, as noted in PatSnap's IP analytics platform.

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Mesoprogestin IP Estate Is Largely Inactive — Freedom to Operate Opportunity

The J-series mesoprogestin IP estate (Jenapharm/Schering/Bayer lineage) is largely inactive, presenting potential freedom-to-operate for next-generation PRM drug programs. The pharmacological distinction between mesoprogestins, full PR antagonists (CDB-4124), and gestagens (dienogest) is IP-distinct — each represents a separate design space. Explore white spaces via PatSnap's customer success case studies.

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Unlock Full Strategic Analysis
Access the complete strategic implications including non-hormonal frontier analysis, immune cell stratification IP, and prolactin/dopamine white-space assessment.
Non-hormonal frontier Precision medicine IP PRLR white-space + Combination strategies
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Emerging Directions

Combination Approaches & Precision Medicine Signals

Retrieved results signal several combination and emerging directions within the endometriosis pipeline. ObsEva's filings across multiple jurisdictions describe dosing schedules that allow temporary cessation of GnRH antagonist to restore hormonal cycling — effectively functioning as an intermittent add-back strategy to reduce bone density effects while maintaining endometriosis suppression.

Endorecherche, Inc. (HK, 2013) claims co-administration of a SERM with LHRH agonists or antagonists, with optional sex steroid precursors (DHEA, DHEA-S), suggesting a multi-target hormonal modulation strategy. Syng Pharmaceuticals explicitly claims that SNCG inhibitors potentiate the efficacy of other hormonal agents — framing this as a combination-eligible mechanism.

A particularly significant emerging direction is CGRP repurposing from migraine. The Children's Medical Center Corporation's 2024 WO filing signals potential repurposing of clinically available CGRP pathway agents (gepants, anti-CGRP antibodies) for endometriosis-associated pain and lesion biology — a direction that could accelerate clinical translation given existing FDA-approved agents in this class. Researchers can track repurposing signals systematically using PatSnap's open API and data integration tools.

Biomarker-stratified therapy selection is an emerging IP battleground. Cedars-Sinai Medical Center (WO/AU, 2024–2026) and Feinstein Institutes for Medical Research (WO/CA/US, 2023–2025) are filing methods for treating endometriosis patients stratified by immune cell compositions (NK cells, T-cells, B-cells) in endometrial tissue — signalling a potential companion diagnostic plus therapeutic co-development opportunity. The PatSnap life sciences intelligence suite supports this kind of multi-modal IP landscape analysis.

Combination Strategies Identified
  • GnRH antagonist + intermittent add-back hormonal therapy (ObsEva)
  • SERM + LHRH agonist/antagonist + DHEA precursors (Endorecherche)
  • SNCG inhibitor + hormonal agent potentiation (Syng Pharmaceuticals)
  • Progesterone antagonist + progestogen sequential regimen (Schering AG)
  • CGRP pathway repurposing from migraine (Children's Medical Center, 2024)
  • Immune cell-stratified patient selection (Cedars-Sinai, Feinstein Institutes)
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Translational Signal

The CGRP/RAMP1 patent (Children's Medical Center, WO 2024) presents quantitative preclinical data: von Frey testing, abdominal contortion frequency, and lesion size measurements across rimegepant, fremanezumab, and galcanezumab in mouse models — representing IND-enabling preclinical evidence for a repurposing strategy.

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Endometriosis Drug Pipeline — Key Questions Answered

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References

  1. GnRH Antagonists for the Treatment of Estrogen-Dependent Disorders — ObsEva S.A., 2021, WO [Patent]
  2. Compositions and Methods for the Treatment of Estrogen-Dependent Disorders — ObsEva S.A., 2021, WO [Patent]
  3. Gonadotropin-Releasing Hormone Antagonist Dosing Regimens for the Treatment of Endometriosis — ObsEva S.A., 2020, AU [Patent]
  4. Compositions and Methods for the Treatment of Adenomyosis and Rectovaginal Endometriosis — ObsEva S.A., 2020, CA [Patent]
  5. Solid Pharmaceutical Formulations for Treating Endometriosis, Uterine Fibroids, Polycystic Ovary Syndrome and Adenomyosis — AbbVie Inc., 2020, IL [Patent]
  6. Pharmaceutical Formulations for Treating Endometriosis, Uterine Fibroids, Polycystic Ovary Syndrome or Adenomyosis — AbbVie Inc., 2020, SG [Patent]
  7. Mesoprogestins for the Treatment and Prevention of Benign Hormone Dependent Gynecological Disorders — Jenapharm GmbH & Co. KG, 2002, EP [Patent]
  8. Mesoprogestins (Progesterone Receptor Modulators) for the Treatment and Prevention of Benign Hormone Dependent Gynecological Disorders — Jenapharm GmbH & Co. KG, 2010, BG [Patent]
  9. Mesoprogestins (Progesterone Receptor Modulators) for the Treatment and Prevention of Benign Hormone Dependent Gynecological Disorders — Schering Aktiengesellschaft, 2001, AU [Patent]
  10. (11β,17β)-17-Hydroxy-11-[4-(methylsulfonyl)phenyl]-17-(pentafluoroethyl)estra-4,9-dien-3-one for the Treatment of Diseases — Bayer Pharma Aktiengesellschaft, 2019, TR [Patent]
  11. Progesterone Antagonists such as CDB-4124 in the Treatment of Endometriosis, Uterine Fibroids, Dysmenorrhea, Breast Cancer — Allergan Pharmaceuticals International Limited, 2012, IL [Patent]
  12. Pharmaceutical Preparation to Reduce Endometriosis — Bayer Schering Parma Aktiengesellschaft, 2009, CR [Patent]
  13. Pharmaceutical Preparation Containing a Gestagen, and Kit and Method for Treating Endometriosis — Zimmermann, Holger, 2008, US [Patent]
  14. Clinical Practice Guidelines for Endometriosis in Japan (The 3rd Edition) — Department of Obstetrics and Gynecology, The University of Tokyo, 2022 [Paper]
  15. Inhibition of Prostaglandin E2 Receptors for the Treatment of Endometriosis — Arosh, Joe A. (Texas A&M University System), 2010, WO [Patent]
  16. Pyrrolidines — Pfizer Limited, 2011, SG [Patent]
  17. Azetidine as an EP2 Antagonist — Pfizer Limited, 2011, JP [Patent]
  18. Compositions for Use in the Treatment of Endometriosis — Yeda Research and Development Company Ltd, 2023, IL [Patent]
  19. CGRP/RAMP1 Blockade to Treat Endometriosis-Associated Pain and Reduce Endometriosis Lesions — The Children's Medical Center Corporation, 2024, WO [Patent]
  20. Inhibitors of IL-11 or IL-11RA for Use in the Treatment of Abnormal Uterine Bleeding — Bayer Aktiengesellschaft, 2022, WO [Patent]
  21. Treatment of Endometriosis — Pfizer Limited, 2010, WO [Patent]
  22. Neutralizing Prolactin Receptor Antibodies and Their Therapeutic Use — Bayer Intellectual Property GmbH, 2017, RS [Patent]
  23. WHO — Endometriosis Fact Sheet [World Health Organization]
  24. NIH — Endometriosis Research and Clinical Information [National Institutes of Health]
  25. FDA — Drug Approvals and Databases: Endometriosis Indications [U.S. Food and Drug Administration]

All data and statistics on this page are sourced from the references above and from PatSnap's proprietary innovation intelligence platform. This page represents a snapshot of innovation signals within the retrieved patent and literature dataset only and should not be interpreted as a comprehensive view of the full clinical pipeline or regulatory landscape.

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