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Recurrent Pericarditis Drug Pipeline — PatSnap Eureka

Recurrent Pericarditis Drug Pipeline — PatSnap Eureka
Recurrent Pericarditis · Drug Pipeline Intelligence

Recurrent Pericarditis Drug Pipeline: IL-1 Inhibitors, Rilonacept & NLRP3 Approaches

The NLRP3 inflammasome and IL-1 signalling axis are driving a new wave of targeted biologics for recurrent pericarditis. Explore patent filings, clinical trial signals, and competitive intelligence — from rilonacept's Phase III RHAPSODY data to emerging NLRP3 small molecules.

Recurrent Pericarditis Drug Pipeline: Development Stages — Rilonacept Phase III, Anakinra Phase II/III RCT, Canakinumab Case Reports, Direct NLRP3 Inhibitors Preclinical, CBD Preclinical, BCP Preclinical Visual summary of six therapeutic modalities targeting IL-1 and NLRP3 pathways in recurrent pericarditis, mapped by clinical development stage from Phase III (rilonacept) to preclinical (CBD, BCP). Source: PatSnap Eureka patent and literature analysis. PIPELINE STAGE OVERVIEW PHASE III Rilonacept (RHAPSODY) PHASE II / RCT Anakinra CASE REPORTS Canakinumab PRECLINICAL NLRP3 SMIs CBD BCP Based on PatSnap Eureka patent & literature dataset · 2019–2025 SMIs = Small Molecule Inhibitors · CBD = Cannabidiol · BCP = Beta-Caryophyllene
15–30%
of acute pericarditis patients develop recurrence
13+
Regeneron patent filings protecting rilonacept in pericarditis
136
IRP patients analysed in landmark autoinflammatory genetics study
11
studies included in 2021 anakinra systematic review
Disease & Target Overview

From Viral Idiopathy to NLRP3-Driven Autoinflammation

Recurrent pericarditis (RP) has been repositioned from a "viral/idiopathic" entity to a disease with clear autoinflammatory underpinnings. The NIH-recognised NLRP3 inflammasome drives cyclical sterile pericardial inflammation, processing pro-IL-1β into its bioactive form via caspase-1 cleavage — making it the central upstream drug target in the field.

Both IL-1α (released by damaged pericardial mesothelial cells) and IL-1β (produced by infiltrating leukocytes after inflammasome activation) are pivotal cytokines. A naturally occurring endogenous antagonist, IL-1 receptor antagonist (IL-1Ra), normally mitigates these effects but is insufficient in RP patients. This dual-cytokine pathophysiology has critical therapeutic implications: agents that block both IL-1α and IL-1β demonstrate clinical superiority over selective IL-1β inhibition.

A genetic analysis from the National Amyloidosis Centre (London), examining 136 IRP patients alongside 1,910 patients with monogenic autoinflammatory diseases, formally linked RP pathogenesis to MEFV, MVK, NLRP3, and TNFRSF1A gene variants — establishing RP within the inflammasome-associated disease spectrum. This precision medicine angle remains an underexplored IP territory. Learn more about PatSnap's life sciences intelligence platform for drug target analysis.

Corticosteroid dependence is the principal unmet-need driver: conventional therapies (NSAIDs, colchicine, corticosteroids) consistently fail a meaningful subset of patients, with corticosteroids paradoxically associated with higher recurrence rates. This failure context motivates the entire IL-1 inhibitor development wave documented in this dataset.

NLRP3
Central inflammasome sensor — top upstream target
IL-1α/β
Dual effector cytokines driving pericardial inflammation
Casp-1
Effector protease downstream of NLRP3 activation
IL-6
Secondary inflammatory mediator; emerging co-target
Key Biomarkers Identified
  • CEACAM1 — proposed serum biomarker
  • MICA/MICB — proposed serum biomarker
  • CRP — primary inflammation endpoint in trials
  • MEFV, NLRP3 gene variants — patient stratification
Therapeutic Modalities

Recurrent Pericarditis Drug Pipeline at a Glance

Seven therapeutic approaches identified across patent filings and peer-reviewed literature, ranked by clinical development stage.

Agent / Approach Mechanism Key Targets Development Stage Lead Assignee
Rilonacept (IL-1 Trap) Soluble IL-1R1/IL-1RAcP-Fc fusion decoy receptor; neutralises IL-1α & IL-1β IL-1α, IL-1β Phase III (RHAPSODY) Regeneron Pharmaceuticals
Anakinra (IL-1Ra) Recombinant IL-1 receptor antagonist; blocks IL-1α & IL-1β at IL-1R1 IL-1R1, IL-1α, IL-1β Phase II / RCT evidence Academic (IRCCS Gaslini, Cleveland Clinic)
Canakinumab (anti-IL-1β mAb) Fully human IgG1κ mAb; selective IL-1β neutralisation only IL-1β Case Reports Novartis (academic evidence)
Direct NLRP3 Inhibitors (INF4E, OLT1177/dapansutrile) Small molecule NLRP3 inflammasome blockade; upstream of IL-1β NLRP3 Preclinical (murine models) VCU Pauley Heart Center (academic)
Cannabidiol (CBD) NLRP3/IL-1β mRNA suppression; IL-6 attenuation; upstream pathway modulator NLRP3, IL-1β, IL-6 Preclinical (in vitro + in vivo) Cardiol Therapeutics Inc.
Beta-Caryophyllene (BCP) Bicyclic sesquiterpene; IL-1β/IL-6 attenuation; reduces pericardial effusion in vivo NLRP3, IL-1β, IL-6 Preclinical (in vitro + in vivo) Cardiol Therapeutics Inc.
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R-Pharm next-gen IL-1 trap PCIS patent claims Wyeth/Pfizer historical IP + more
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Data Visualisation

Patent Activity & Clinical Evidence Signals

Key data points from the PatSnap Eureka patent and literature dataset for recurrent pericarditis, 2019–2025.

Patent Filings by Assignee — Recurrent Pericarditis (2019–2025)

Regeneron dominates with 13+ filings across US, EP, CA, and WO jurisdictions; Cardiol Therapeutics and R-Pharm are emerging challengers.

Patent Filings by Assignee in Recurrent Pericarditis 2019–2025: Regeneron 13+, Cardiol Therapeutics 4, R-Pharm Overseas 1 Bar chart showing patent filing counts for key assignees in the recurrent pericarditis space. Regeneron Pharmaceuticals leads with at least 13 filings protecting the IL-1R/IL-1RAcP-Fc fusion protein. Source: PatSnap Eureka patent analysis, 2019–2025. 14 10 7 3 0 13+ Regeneron 4 Cardiol Therapeutics 1 R-Pharm Overseas

IL-1 Target Coverage: Dual vs. Selective Blockade

Clinical evidence favours dual IL-1α+β blockade (anakinra, rilonacept) over selective IL-1β inhibition (canakinumab) in recurrent pericarditis.

IL-1 Target Coverage in RP Agents: Dual IL-1α+β blockade (Rilonacept, Anakinra) vs Selective IL-1β only (Canakinumab) — dual blockade clinically superior per retrieved evidence Comparison of IL-1 cytokine targeting strategies across approved and investigational agents in recurrent pericarditis. Retrieved clinical evidence from Cleveland Clinic and IRCCS Gaslini indicates that dual IL-1α and IL-1β blockade produces superior outcomes versus selective IL-1β inhibition. Source: PatSnap Eureka literature analysis. Dual IL-1α + IL-1β Rilonacept · Anakinra Clinically superior in RP vs Selective IL-1β only Canakinumab Relapses observed in paediatric RP

Clinical Evidence Timeline — IL-1 Inhibitors in RP

From first paediatric anakinra case reports (2008) through Phase III RHAPSODY data (2022), showing the evidence build over 14 years.

Clinical Evidence Timeline for IL-1 Inhibitors in Recurrent Pericarditis: 2008 first anakinra paediatric case, 2013 early cohort data, 2017 review evidence, 2020 rilonacept Phase II, 2021 anakinra RCT, 2022 Phase III RHAPSODY published Timeline of key clinical milestones for IL-1 inhibitors in recurrent pericarditis from 2008 to 2022, derived from PatSnap Eureka literature analysis. Shows progression from case reports to Phase III randomised controlled trial evidence for rilonacept. 2008 Anakinra Case Report 2013 Anakinra Early Cohort 2017 IL-1 Role Review 2020 Rilonacept Phase II 2021 Anakinra RCT Data 2022 RHAPSODY Phase III Source: PatSnap Eureka literature dataset · IRCCS Gaslini, Cleveland Clinic, Mayo Clinic publications

NLRP3 Pathway: Drug Intervention Points in Recurrent Pericarditis

Five intervention points identified across retrieved patent and literature records, from upstream DAMP sensing to downstream cytokine signalling.

NLRP3 Pathway Intervention Points in Recurrent Pericarditis: DAMPs trigger NLRP3 assembly → Caspase-1 activation → pro-IL-1β cleavage → IL-1α/IL-1β release → IL-1R1 signalling → inflammation. Drug targets: NLRP3 (INF4E, OLT1177, CBD, BCP), Caspase-1, IL-1β (canakinumab), IL-1α+β (rilonacept, anakinra), IL-1R1 (anakinra) Process diagram showing the NLRP3 inflammasome signalling cascade in recurrent pericarditis pericardial tissue, with annotated drug intervention points for each therapeutic modality identified in the PatSnap Eureka dataset. Source: VCU Pauley Heart Center, ASST Sette Laghi Varese, Cleveland Clinic literature records. Pericardial DAMPs Injury signal NLRP3 Inflammasome CBD · BCP · INF4E ↑ Drug target Caspase-1 Cleavage of pro-IL-1β IL-1α + IL-1β Release Rilonacept · Anakinra ↑ Drug target IL-1R1 Signalling Pericardial Inflammation Source: VCU Pauley Heart Center · ASST Sette Laghi Varese · Cleveland Clinic — PatSnap Eureka dataset

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Therapeutic Modalities Deep Dive

IL-1 Inhibitors: Mechanistic Differentiation & Clinical Evidence

Three primary IL-1 pathway agents — each with distinct mechanisms and evidence bases — define the current commercial and clinical landscape for recurrent pericarditis.

Phase III · Commercial

Rilonacept (IL-1 Trap) — Regeneron Pharmaceuticals

A soluble chimeric fusion protein combining IL-1R1 and IL-1RAcP extracellular domains linked to an Fc region. Acts as a high-affinity decoy receptor neutralising both IL-1α and IL-1β. Phase II data (Cleveland Clinic/Mayo Clinic) showed rapid CRP normalisation and pain resolution with 320 mg SC loading dose and 160 mg SC weekly maintenance. The pivotal Phase III RHAPSODY trial is referenced across multiple retrieved papers as demonstrating rapid pain and inflammation resolution with markedly reduced recurrence and a favourable safety profile. Regeneron holds 13+ active or pending patents across US, EP, CA, and WO jurisdictions (2019–2025), signalling aggressive IP lifecycle management. Explore PatSnap's IP analytics tools for competitive patent landscaping.

Dual IL-1α + IL-1β neutralisation
Phase II / RCT · Academic

Anakinra (IL-1Ra) — Recombinant IL-1 Receptor Antagonist

A recombinant human IL-1 receptor antagonist that competitively blocks both IL-1α and IL-1β signalling at IL-1R1. The most extensively documented agent in academic literature, with evidence spanning case reports, multicenter cohort analyses, and randomised controlled trials. A 2021 systematic review (California Institute of Behavioral Neurosciences) found 100 mg/day produced "remarkable improvement in patient outcomes" across 11 studies. Early paediatric use was documented as early as 2008 at IRCCS G. Gaslini (Genoa). Consistently described as rapidly acting, steroid-sparing, and safe. Multiple retrieved papers cite a completed RCT, distinguishing anakinra from canakinumab which has not been tested in a randomised RP trial. According to the EMA, IL-1 receptor antagonism is a validated mechanism in autoinflammatory conditions.

Steroid-sparing · Rapidly acting
Case Reports Only · Selective IL-1β

Canakinumab — Selective Anti-IL-1β Monoclonal Antibody

A fully human IgG1κ monoclonal antibody selectively neutralising IL-1β without affecting IL-1α. A critical 2020 paediatric case report from IRCCS Istituto Giannina Gaslini describes two children who responded well to anakinra but relapsed promptly upon switching to canakinumab — suggesting that simultaneous IL-1α and IL-1β blockade may be necessary for adequate RP disease control. This finding directly supports the mechanistic superiority of dual-targeting agents (rilonacept, anakinra) in RP. No randomised controlled trial data specifically in RP is available in retrieved results. The WHO essential medicines framework recognises IL-1 inhibition in autoinflammatory disease management.

IL-1β selective — insufficient in RP
Preclinical · Patent Stage

Cannabidiol & Beta-Caryophyllene — Cardiol Therapeutics Inc.

Two distinct Cardiol Therapeutics patent families (WO 2024, US pending 2026, AU pending 2025) disclose cannabidiol (CBD) and beta-caryophyllene (BCP) for treating or preventing recurrent pericarditis. CBD patents claim attenuation of IL-1β and IL-6 levels, suppression of pro-IL-1β and NLRP3 mRNA transcription in vitro, and prevention of pericardial space increases in murine models. BCP (a bicyclic sesquiterpene) claims similar in vitro IL-1β/IL-6 attenuation and in vivo reduction of pericardial effusion and thickening. These represent the most recently dated patents (2024–2026) in this RP dataset and position natural compound-derived NLRP3 modulators as a potential oral/non-injectable alternative to injectable biologics. The PatSnap customer case studies include examples of early-stage biotech IP strategy in emerging therapeutic areas.

Oral/non-injectable NLRP3 modulation
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Strategic Intelligence

Competitive & IP Landscape: Strategic Implications

Key strategic signals extracted from patent filings and clinical literature for biopharma teams, IP counsel, and investors evaluating the recurrent pericarditis space.

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Regeneron's IP Position Is the Most Defensible

With 13+ patent filings across US, EP, CA, and WO jurisdictions spanning 2019–2025, Regeneron's IL-1R/IL-1RAcP-Fc fusion protein mechanism for pericarditis and PCIS creates substantial freedom-to-operate challenges for competitors seeking to enter with similar IL-1 trap molecules. US filings range from active granted patents to pending continuations as late as November 2025, indicating sustained portfolio extension activity.

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Dual IL-1α+β Blockade Is the Mechanistic Standard

Retrieved results consistently frame rilonacept and anakinra as superior to canakinumab in RP due to dual-cytokine neutralisation. The canakinumab failure signal (paediatric relapses upon switch from anakinra) provides direct clinical evidence. Drug developers targeting RP should prioritise dual-blocking molecules or provide explicit mechanistic rationale if pursuing IL-1β-selective strategies.

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Emerging Directions

Combination Approaches & Next-Generation Strategies

Biologic + corticosteroid weaning protocols are the dominant real-world translational model. Multiple retrieved papers describe clinical protocols where IL-1 inhibitors (anakinra or rilonacept) are introduced to enable tapering and cessation of corticosteroids in steroid-dependent patients. The Phase II rilonacept trial specifically included a corticosteroid-dependent cohort with a structured wean protocol.

NLRP3-targeted small molecules in cardiovascular disease are advancing in adjacent indications. Retrieved papers discuss direct NLRP3 inhibitors (INF4E, OLT1177/dapansutrile, IZD334) in cardiac ischaemia-reperfusion and heart failure models. VCU data demonstrates that NLRP3 blockers reduce pericardial inflammation in animal models alongside IL-1 biologics — suggesting upstream NLRP3 inhibition as a future oral RP strategy. PatSnap's patent analytics platform enables freedom-to-operate analysis for novel NLRP3 inhibitor chemical series.

Natural compound NLRP3 modulators from Cardiol Therapeutics Inc. (cannabidiol, BCP, filed 2024–2026) represent the most recently dated RP-specific patents in this dataset. These claim in vitro NLRP3 mRNA suppression and in vivo pericardial effusion reduction — positioning them as early preclinical bets on oral/non-injectable alternatives to injectable biologics. Investors should monitor NLRP3 mRNA suppression claims as a mechanistic validation endpoint.

Autoinflammatory genotyping to guide therapy is an emerging precision medicine direction. Genetic screening for MEFV, NLRP3, and related autoinflammatory variants may identify which patients are most likely to respond to IL-1 inhibition. The European Bioinformatics Institute maintains variant databases relevant to this stratification approach. This direction is not yet formalised in retrieved clinical trial protocols but is increasingly discussed in academic literature — and remains an underexplored IP territory. See how PatSnap's life sciences solutions support precision medicine IP strategy.

Emerging Pipeline Signals
  • Biologic-enabled corticosteroid tapering protocols
  • Oral NLRP3 small molecule inhibitors (preclinical)
  • CBD and BCP as NLRP3 mRNA suppressors
  • R-Pharm heterodimeric IL-1 trap (next-gen)
  • Autoinflammatory genotyping for patient stratification
  • IL-6 as emerging co-target (CBD, BCP patents)
Key Assignee Watch List
Regeneron Pharmaceuticals 13+ patents
Cardiol Therapeutics Inc. 4 filings (2024–26)
R-Pharm Overseas Inc. 1 pending (2024)
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Frequently Asked Questions

Recurrent Pericarditis Drug Pipeline — Key Questions Answered

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References

  1. Emerging Therapies for Recurrent Pericarditis: Interleukin-1 inhibitors — University Cardiology, A.O.U. Città della Salute e della Scienza di Torino, 2021
  2. Interleukin-1 Antagonists for the Treatment of Recurrent Pericarditis — Cleveland Clinic, 2022
  3. Novel Pharmacotherapies for Recurrent Pericarditis: Current Options in 2020 — Fatebefratelli Hospital, Milan, 2020
  4. Rilonacept and Anakinra in Recurrent Pericarditis: A Systematic Review and Meta-Analysis — Hawler Medical University, 2022
  5. Anti-interleukin-1 agents for pericarditis: a primer for cardiologists — Cleveland Clinic, 2021
  6. Interleukin-1 and the NLRP3 Inflammasome in Pericardial Disease — ASST Sette Laghi, Varese, 2021
  7. Recurrent Pericarditis: a Stubborn Opponent Meets New Treatments in 2022 — University of Vermont, 2022
  8. Rilonacept (Interleukin-1 Inhibition) for the Treatment of Pericarditis — Cleveland Clinic, 2022
  9. Efficacy of Anakinra in Pericarditis: A Systematic Review — California Institute of Behavioral Neurosciences & Psychology, 2022
  10. The Role of NLRP3 Inflammasome in Pericarditis — VCU Pauley Heart Center, 2021
  11. Efficacy and safety of rilonacept for recurrent pericarditis: results from a phase II clinical trial — Mayo Clinic / Cleveland Clinic, 2020
  12. Treatment of inflammatory conditions by delivery of interleukin-1 receptor antagonist fusion protein — Regeneron Pharmaceuticals, Inc., 2022, US [Patent]
  13. Treatment of inflammatory conditions by delivery of interleukin-1 receptor antagonist fusion protein — Regeneron Pharmaceuticals, Inc., 2019, CA [Patent]
  14. Treatment of inflammatory conditions by delivery of interleukin-1 receptor antagonist fusion protein — Regeneron Pharmaceuticals, Inc., 2019, WO [Patent]
  15. Treatment of recurrent idiopathic pericarditis by delivery of interleukin-1 receptor antagonist fusion protein — Regeneron Pharmaceuticals, Inc., 2025, EP [Patent]
  16. Use of il1-r1 derived inhibitor of il-1b for the treatment of idiopathic recurrent pericarditis — R-Pharm Overseas, Inc., 2024, US [Patent]
  17. Cannabidiol for use in treating or preventing recurrent pericarditis — Cardiol Therapeutics Inc., 2024, WO [Patent]
  18. Beta-caryophyllene for use in treating or preventing pericarditis — Cardiol Therapeutics Inc., 2024, WO [Patent]
  19. IL-1 beta receptor antagonist efficacy in the treatment of idiopathic recurrent pericarditis — IRCCS G. Gaslini, 2008
  20. Failure of anti Interleukin-1β monoclonal antibody in the treatment of recurrent pericarditis in two children — IRCCS Istituto Giannina Gaslini, 2020
  21. National Institutes of Health (NIH) — Autoinflammatory Disease Research
  22. European Medicines Agency (EMA) — IL-1 Receptor Antagonism in Autoinflammatory Conditions
  23. World Health Organization (WHO) — Essential Medicines Framework: Autoinflammatory Disease Management
  24. European Bioinformatics Institute (EBI) — Autoinflammatory Gene Variant Databases (MEFV, NLRP3, MVK, TNFRSF1A)

All data and statistics on this page are sourced from the references above and from PatSnap's proprietary innovation intelligence platform. This report is derived from a limited set of patent and literature records retrieved across targeted searches and represents a snapshot of innovation signals within this dataset only — it should not be interpreted as a comprehensive view of the full field, clinical pipeline, or regulatory landscape.

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